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NPC Registry (AC-056C501) Registry is an international, multi-center, prospective, observational, long-term project for patients diagnosed with NP-C

NPC Registry (AC-056C501) Registry is an international, multi-center, prospective, observational, long-term project for patients diagnosed with NP-C


CSR Summary

Not Available


NCT Number

Not Available


Data Specification

Not Available


Annotated CRF

Not Available

Product Info

Generic Name
Miglustat
Product Name
ZAVESCA®
Therapeutic Area
Pulmonary Hypertension
Enrollment
472
% Female
48.1%
% White
N/A
Product Class
Metabolic Modifier
Sponsor Protocol Number
AC-056C501
Data Partner
Johnson & Johnson
Condition Studied
Niemann-Pick Type C Disease
Mean/Median Age (Years)
21.2

Supporting Documentation

Clinical Study Report
Collected Datasets
Protocol with Amendments

Disclaimer

Clinical study data provided through this site do not replace the official labeling of a given drug product, which presents benefits and risks of the product for approved use(s). Before prescribing any product, health care professionals should consult the current prescribing information approved in their country. Patients seeking information may consult with their health care professional about the product, for which health authority approved written patient information may be available.