NPC Registry (AC-056C501) Registry is an international, multi-center, prospective, observational, long-term project for patients diagnosed with NP-C

  • PDF icon for CSR Summary CSR Summary Not Available
  • Globe symbol for NCT Number NCT Number Not Available
  • Notebook for Primary Citation Primary Citation
  • Spreadsheet for Data Specification Data Specification Not Available

Trial Information

Generic NameMiglustatProduct NameZAVESCA®Therapeutic AreaPulmonary HypertensionEnrollment472% Female48.1%% WhiteN/A
Product ClassMetabolic ModifierSponsor Protocol NumberAC-056C501Data PartnerJohnson & JohnsonCondition StudiedNiemann-Pick Type C DiseaseMean/Median Age (Years)21.2

Supporting Documentation

  • Collected Datasets Available
  • Protocol with Amendments Available
  • Clinical Study Report Available

Approved Data Requests Associated with this Trial

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