NPC Registry (AC-056C501) is an international, multi-center, prospective, observational, long-term project for patients diagnosed with NP-C

  • PDF icon for CSR Summary CSR Summary Not Yet Available
  • Globe symbol for NCT Number NCT Number Not Available
  • Notebook for Primary Citation Primary Citation
  • Spreadsheet for Data Specification Data Specification Not Available

Trial Information

Generic NameMiglustatProduct NameZAVESCA®Therapeutic AreaAlimentary Tract and MetabolismProduct ClassOther Alimentary Tract and Metabolism ProductsCondition StudiedNiemann-Pick Type C DiseaseChemical SubgroupsN/APharmacological SubgroupsN/A
Sponsor Protocol NumberAC-056C501Enrollment472Data PartnerJohnson & Johnson% Female48.1%Mean/Median Age (Years)21.2% WhiteN/A

Supporting Documentation

  • Collected Datasets Available
  • Protocol with Amendments Available
  • Clinical Study Report Available

Approved Data Requests Associated with this Trial

Disclaimer

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