NPC Registry (AC-056C501) Registry is an international, multi-center, prospective, observational, long-term project for patients diagnosed with NP-C

  • 1 CSR Summary Not Available
  • 1 NCT Number Not Available
  • 1 Primary Citation
  • Data Specification Not Available

Trial Information

Generic NameMiglustatProduct NameZAVESCA®Therapeutic AreaPulmonary HypertensionEnrollment472% Female48.1%% WhiteN/A
Product ClassMetabolic ModifierSponsor Protocol NumberAC-056C501Data PartnerJohnson & JohnsonCondition StudiedNiemann-Pick Type C DiseaseMean/Median Age (Years)21.2

Supporting Documentation

  • Collected Datasets Available
  • Protocol with Amendments Available
  • Clinical Study Report Available

Approved Data Requests Associated with this Trial

Disclaimer

Clinical study data provided through this site do not replace the official labeling of a given drug product, which presents benefits and risks of the product for approved use(s). Before prescribing any product, health care professionals should consult the current prescribing information approved in their country. Patients seeking information may consult with their health care professional about the product, for which health authority approved written patient information may be available.